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Intrathecal/intracerebroventricular enzyme replacement therapy for the mucopolysaccharidoses: efficacy, safety and prospects
Giugliani, Roberto, Dalla Corte, Amauri, Poswar, Fabiano, Vanzella, Cláudia, Horovitz, Dafne, Riegel, Mariluce, Baldo, Guilherme, Vairo, FilippoLanguage:
english
Journal:
Expert Opinion on Orphan Drugs
DOI:
10.1080/21678707.2018.1487838
Date:
June, 2018
File:
PDF, 1004 KB
english, 2018