Transatlantic combined and comparative data analysis of 1095 patients with urea cycle disorders—a successful strategy for clinical research of rare diseases
Posset, Roland, Garbade, Sven F., Boy, Nikolas, Burlina, Alberto B., Dionisi-Vici, Carlo, Dobbelaere, Dries, Garcia-Cazorla, Angeles, de Lonlay, Pascale, Teles, Elisa Leão, Vara, Roshni, Ah Mew, NichoLanguage:
english
Journal:
Journal of Inherited Metabolic Disease
DOI:
10.1007/s10545-018-0222-z
Date:
July, 2018
File:
PDF, 993 KB
english, 2018