Efficacy and safety of intrathecal idursulfase in pediatric...

Molecular Genetics and Metabolism 2018 / 02 Vol. 123; Iss. 2

Efficacy and safety of intrathecal idursulfase in pediatric patients with mucopolysaccharidosis type II and early cognitive impairment: Design and methods of a controlled, randomized, phase II/III multicenter study

Muenzer, Joseph, Burton, Barbara K., Harmatz, Paul, Gutiérrez-Solana, Luis González, Ruiz-Garcia, Matilde, Jones, Simon A., Guffon, Nathalie, Inbar-Feigenberg, Michal, Bratkovic, Drago, Wu, Yuna, Alex
How much do you like this book?
What’s the quality of the file?
Download the book for quality assessment
What’s the quality of the downloaded files?
Volume:
123
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.12.262
Date:
February, 2018
File:
PDF, 75 KB
english, 2018
Conversion to is in progress
Conversion to is failed