Outcome measures for children with mitochondrial disease: consensus recommendations for future studies from a Delphi-based international workshop
Koene, Saskia, van Bon, Lara, Bertini, Enrico, Jimenez-Moreno, Cecilia, van der Giessen, Lianne, de Groot, Imelda, McFarland, Robert, Parikh, Sumit, Rahman, Shamima, Wood, Michelle, Zeman, Jiri, JanssLanguage:
english
Journal:
Journal of Inherited Metabolic Disease
DOI:
10.1007/s10545-018-0229-5
Date:
July, 2018
File:
PDF, 414 KB
english, 2018