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Use of modified U1 small nuclear RNA for rescue from exon 7 skipping caused by 5′-splice site mutation of human cathepsin A gene
Yamazaki, Naoshi, Kanazawa, Keisuke, Kimura, Maria, Ike, Hironobu, Shinomiya, Makiko, Tanaka, Shouko, Shinohara, Yasuo, Minakawa, Noriaki, Itoh, Kohji, Takiguchi, YoshiharuVolume:
677
Language:
english
Journal:
Gene
DOI:
10.1016/j.gene.2018.07.030
Date:
November, 2018
File:
PDF, 916 KB
english, 2018