Clinical effectiveness of enzyme replacement therapy with galsulfase in mucopolysaccharidosis type VI treatment: systematic review
Gomes, Dalila Fernandes, Gallo, Luciana Guerra, Leite, Betânia Ferreira, Silva, Roberta Borges, da Silva, Everton NunesJournal:
Journal of Inherited Metabolic Disease
DOI:
10.1007/s10545-018-0242-8
Date:
August, 2018
File:
PDF, 527 KB
2018