Preclinical Evaluation of Efficacy and Safety of an Improved Lentiviral Vector for the Treatment of β-Thalassemia and Sickle Cell Disease
Negre, Olivier, Bartholomae, Cynthia, Beuzard, Yves, Cavazzana, Marina, Christiansen, Lauryn, Courne, Celine, Deichmann, Annette, Denaro, Maria, Dreuzy, Edouard, Finer, Mitchell, Fronza, Raffaele, GilVolume:
15
Language:
english
Journal:
Current Gene Therapy
DOI:
10.2174/1566523214666141127095336
Date:
December, 2014
File:
PDF, 664 KB
english, 2014