An ex-vivo RNA trans -splicing strategy to correct human generalized severe epidermolysis bullosa simplex
Peking, P., Breitenbach, J.S., Ablinger, M., Muss, W.H., Poetschke, F.J., Kocher, T., Koller, U., Hainzl, S., Kitzmueller, S., Bauer, J.W., Reichelt, J., Lettner, T., Wally, V.Language:
english
Journal:
British Journal of Dermatology
DOI:
10.1111/bjd.17075
Date:
August, 2018
File:
PDF, 639 KB
english, 2018