Preclinical development of a hematopoietic stem and progenitor cell bioengineered factor VIII lentiviral vector gene therapy for hemophilia A
Doering, Christopher B, Denning, Gabriela, Shields, Jordan, Fine, Eli J, Parker, Ernest T, Srivastava, Alok, Lollar, Pete, Spencer, H. TrentLanguage:
english
Journal:
Human Gene Therapy
DOI:
10.1089/hum.2018.137
Date:
August, 2018
File:
PDF, 4.14 MB
english, 2018