Development of methodology and study protocol: Safety and efficacy of a single subretinal injection of rAAV.hCNGA3 in patients with CNGA3-linked achromatopsia investigated in an exploratory dose-escalation trial
Kahle, Nadine Andrea, Peters, Tobias, Zobor, Ditta, Kuehlewein, Laura, Kohl, Susanne, Zhour, Ahmad, Werner, Annette, Seitz, Immanuel Philipp, Sothilingam, Vithiyanjali, Michalakis, Stylianos, Biel, MaLanguage:
english
Journal:
Human Gene Therapy Clinical Development
DOI:
10.1089/humc.2018.088
Date:
September, 2018
File:
PDF, 8.22 MB
english, 2018