Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD
Akpulat, Ugur, Wang, Haicui, Becker, Kerstin, Contreras, Adriana, Partridge, Terence A., Novak, James S., Cirak, SebahattinVolume:
13
Language:
english
Journal:
Molecular Therapy - Nucleic Acids
DOI:
10.1016/j.omtn.2018.10.002
Date:
December, 2018
File:
PDF, 1.46 MB
english, 2018