MO068EFFICACY AND SAFETY OF MIGALASTAT, AN ORAL PHARMACOLOGICAL CHAPERONE FOR FABRY DISEASE: RENAL FINDINGS FROM TWO RANDOMIZED PHASE 3 STUDIES (FACETS AND ATTRACT)
Schiffmann, Raphael, Nicholls, Kathleen, Bichet, Daniel, Feldt-Rasmussen, Ulla, Jovanovic, Ana, Hughes, Derralynn, Jain, Vipul, Castelli, Jeffrey, Skuban, Nina, Barth, JayVolume:
32
Language:
english
Journal:
Nephrology Dialysis Transplantation
DOI:
10.1093/ndt/gfx126
Date:
May, 2017
File:
PDF, 69 KB
english, 2017