Nonsense-mediated mRNA decay efficiency varies in choroideremia providing a target to boost small molecule therapeutics
Sarkar, Hajrah, Mitsios, Andreas, Smart, Matthew, Skinner, Jane, Welch, Ailsa, Kalatzis, Vasiliki, Coffey, Pete, Dubis, Adam M, Webster, Andrew, Moosajee, MariyaJournal:
Human Molecular Genetics
DOI:
10.1093/hmg/ddz028
Date:
January, 2019
File:
PDF, 681 KB
2019