Erythroid-Progenitor-Targeted Gene Therapy Using Bifunctional TFR1 Ligand-Peptides in Human Erythropoietic Protoporphyria
Mirmiran, Arienne, Schmitt, Caroline, Lefebvre, Thibaud, Manceau, Hana, Daher, Raêd, Oustric, Vincent, Poli, Antoine, Lacapère, Jean-Jacques, Moulouel, Boualem, Puy, Hervé, Karim, Zoubida, Peoc'h, KatJournal:
The American Journal of Human Genetics
DOI:
10.1016/j.ajhg.2018.12.021
Date:
January, 2019
File:
PDF, 1.06 MB
2019