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ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome
Ou, Li, DeKelver, Russell C., Rohde, Michelle, Tom, Susan, Radeke, Robert, St. Martin, Susan J., Santiago, Yolanda, Sproul, Scott, Przybilla, Michelle J., Koniar, Brenda L., Podetz-Pedersen, Kelly M.,Volume:
27
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2018.10.018
Date:
January, 2019
File:
PDF, 1.51 MB
english, 2019