Persistent treatment effect of cerliponase alfa in children...

Molecular Genetics and Metabolism 2019 / 02 Vol. 126; Iss. 2

Persistent treatment effect of cerliponase alfa in children with CLN2 disease: A 3 year update from an ongoing multicenter extension study

Schulz, Angela, Specchio, Nicola, Gissen, Paul, de los Reyes, Emily, Cahan, Heather, Slasor, Peter, Jacoby, David, Ajayi, Temitayo
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Volume:
126
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.342
Date:
February, 2019
File:
PDF, 45 KB
english, 2019
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