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Pharmacological and clinical profile of spinal muscular atrophy (SMA) therapeutic drug nusinersen (Spinraza®); 脊髄性筋萎縮症(SMA)治療薬ヌシネルセン(スピンラザ®)の薬理学的特徴と臨床試験成績;
Ohmura, Tsuyoshi, Saeki, Seiji, Ogiwara, Kazutaka, Tobita, Kimimasa, Ling, Yan, Torii, ShinichiVolume:
152
Year:
2018
Journal:
Folia Pharmacologica Japonica
DOI:
10.1254/fpj.152.147
File:
PDF, 1.47 MB
2018