Allele-Specific CRISPR/Cas9 Correction of a Heterozygous DNM2 Mutation Rescues Centronuclear Myopathy Cell Phenotypes
Rabai, Aymen, Reisser, Léa, Reina-San-Martin, Bernardo, Mamchaoui, Kamel, Cowling, Belinda S., Nicot, Anne-Sophie, Laporte, JocelynVolume:
16
Journal:
Molecular Therapy - Nucleic Acids
DOI:
10.1016/j.omtn.2019.02.019
Date:
June, 2019
File:
PDF, 1.79 MB
2019