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The alpha-1-antitrypsin promoter improves the efficacy of an AAV vector for the treatment of MNGIE
Cabrera-Pérez, Raquel, Vila-Julia, Ferran, Hirano, Michio, Mingozzi, Federico, Torres-Torronteras, Javier, Marti, RamonLanguage:
english
Journal:
Human Gene Therapy
DOI:
10.1089/hum.2018.217
Date:
March, 2019
File:
PDF, 1.55 MB
english, 2019