Evaluating the Impact of Variable Phosphorothioate Content in Tricyclo-DNA Antisense Oligonucleotides in a Duchenne Muscular Dystrophy Mouse Model
Echevarría, Lucía, Aupy, Philippine, Relizani, Karima, Bestetti, Thomas, Griffith, Graziella, Blandel, Florence, Komisarski, Marek, Haeberli, Adrian, Svinartchouk, Fedor, Garcia, Luis, Goyenvalle, AurJournal:
Nucleic Acid Therapeutics
DOI:
10.1089/nat.2018.0773
Date:
April, 2019
File:
PDF, 717 KB
2019