Enzyme replacement therapy in patients with mucopolysaccharidosis type VI: Updated findings from the MPS VI clinical surveillance program
Harmatz, Paul, Lampe, Christina, Parini, Rossella, Sharma, Reena, Leão-Teles, Elisa, Johnson, Julie, Sivam, Debbie, Sisic, ZlatkoVolume:
126
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.162
Date:
February, 2019
File:
PDF, 52 KB
english, 2019