Impact of two-year elosulfase alfa treatment on patient-reported outcomes in patients with Morquio syndrome type A: Results from an English managed access agreement
Adam, Jacqueline, Cleary, Maureen, Hendriksz, Christian, Geberhiwot, Tarekegn, Hughes, Derralynn, Jones, Simon A., Jovanovic, Ana, Morrison, Alexandra, Murphy, Elaine, Vijay, SureshVolume:
126
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.022
Date:
February, 2019
File:
PDF, 46 KB
english, 2019