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Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina
Tornabene, Patrizia, Trapani, Ivana, Minopoli, Renato, Centrulo, Miriam, Lupo, Mariangela, de Simone, Sonia, Tiberi, Paola, Dell’Aquila, Fabio, Marrocco, Elena, Iodice, Carolina, Iuliano, Antonella, GVolume:
11
Language:
english
Journal:
Science Translational Medicine
DOI:
10.1126/scitranslmed.aav4523
Date:
May, 2019
File:
PDF, 8.55 MB
english, 2019