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Healthcare resource use in severe mucopolysaccharidosis type I post-transplant children via parent survey
Conner, Therese, Cook, Francesca, Fernandez, Vivian, Rangel-Miller, Vanessa, Rascati, KarenVolume:
126
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.087
Date:
February, 2019
File:
PDF, 66 KB
2019