Migalastat reduces globotriaosylceramide (GL-3) inclusions...

Migalastat reduces globotriaosylceramide (GL-3) inclusions in renal peritubular capillaries in patients with Fabry disease and migalastat-amenable mutations: Post hoc analyses from FACETS

Barisoni, Laura M., Charles Jennette, J., Skuban, Nina, Castelli, Jeffery P., Colvin, Robert B.
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Volume:
126
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.048
Date:
February, 2019
File:
PDF, 51 KB
2019
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