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AAV9.LAMP-2B IMPROVES METABOLIC AND PHYSIOLOGIC FUNCTION IN MURINE AND HUMAN IN-VITRO MODELS OF DANON DISEASE
Adler, Eric, Gault, Emily, Villarruel, Eliza, Hashem, Sherin, Nelson, Bradley, Manso, Ana MariaVolume:
73
Language:
english
Journal:
Journal of the American College of Cardiology
DOI:
10.1016/S0735-1097(19)31295-1
Date:
March, 2019
File:
PDF, 163 KB
english, 2019