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In vitro validation of a CRISPR-mediated CFTR correction strategy for preclinical translation in pigs
Zhou, Zhichang Peter, Yang, Liang Leo, Cao, Huibi, Chen, Ziyan Rachel, Zhang, Yiqian, Wen, Xian-Yan, Hu, JimJournal:
Human Gene Therapy
DOI:
10.1089/hum.2019.074
Date:
May, 2019
File:
PDF, 2.04 MB
2019