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Targeted Transgene Activation in the Brain Tissue by Systemic Delivery of Engineered AAV1 Expressing CRISPRa
Lau, Cia-Hin, Ho, Jonathan Weng-Thim, Lo, Pik Kwan, Tin, ChungVolume:
16
Journal:
Molecular Therapy - Nucleic Acids
DOI:
10.1016/j.omtn.2019.04.015
Date:
June, 2019
File:
PDF, 2.44 MB
2019