![](/img/cover-not-exists.png)
Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study
Klopstock, Thomas, Tricta, Fernando, Neumayr, Lynne, Karin, Ivan, Zorzi, Giovanna, Fradette, Caroline, Kmieć, Tomasz, Büchner, Boriana, Steele, Hannah E, Horvath, Rita, Chinnery, Patrick F, Basu, AnnaVolume:
18
Language:
english
Journal:
The Lancet Neurology
DOI:
10.1016/S1474-4422(19)30142-5
Date:
July, 2019
File:
PDF, 865 KB
english, 2019