Therapeutic efficacy and safety of scAAV9/AGA gene therapy in aspartylglucosaminuria mice
Chen, Xin, Snanoudj-Verber, Sarah, Pollard, Laura, Cathey, Sara, Gray, Steven J.Volume:
126
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.078
Date:
February, 2019
File:
PDF, 46 KB
2019