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Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease
Zeitler, Bryan, Froelich, Steven, Marlen, Kimberly, Shivak, David A, Yu, Qi, Li, Davis, Pearl, Jocelynn R, Miller, Jeffrey C, Zhang, Lei, Paschon, David E, Hinkley, Sarah J, Ankoudinova, Irina, Lam, SLanguage:
english
Journal:
Nature Medicine
DOI:
10.1038/s41591-019-0478-3
Date:
July, 2019
File:
PDF, 21.29 MB
english, 2019