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Investigational RNAi Therapeutic Targeting C5 Is Efficacious in Pre-clinical Models of Myasthenia Gravis
Kusner, Linda L., Yucius, Kristina, Sengupta, Manjistha, Sprague, Andrew G., Desai, Dhruv, Nguyen, Tuyen, Charisse, Klaus, Kuchimanchi, Satya, Kallanthottathil, Rajeev, Fitzgerald, Kevin, Kaminski, HeVolume:
13
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2019.04.009
Date:
June, 2019
File:
PDF, 1.41 MB
2019