From Clinical Trials to Clinical Practice: Practical Considerations for Gene Replacement Therapy in SMA Type 1
Al-Zaidy, Samiah A., Mendell, Jerry R.Language:
english
Journal:
Pediatric Neurology
DOI:
10.1016/j.pediatrneurol.2019.06.007
Date:
June, 2019
File:
PDF, 451 KB
english, 2019