Pharmacological enhancement of KCC2 gene expression exerts therapeutic effects on human Rett syndrome neurons and Mecp2 mutant mice
Tang, Xin, Drotar, Jesse, Li, Keji, Clairmont, Cullen D., Brumm, Anna Sophie, Sullins, Austin J., Wu, Hao, Liu, Xiaoxiao Shawn, Wang, Jinhua, Gray, Nathanael S., Sur, Mriganka, Jaenisch, RudolfVolume:
11
Language:
english
Journal:
Science Translational Medicine
DOI:
10.1126/scitranslmed.aau0164
Date:
July, 2019
File:
PDF, 6.93 MB
english, 2019