Therapeutically relevant engraftment of a CRISPR-Cas9–edited HSC-enriched population with HbF reactivation in nonhuman primates
Humbert, Olivier, Radtke, Stefan, Samuelson, Clare, Carrillo, Ray R., Perez, Anai M., Reddy, Sowmya S., Lux, Christopher, Pattabhi, Sowmya, Schefter, Lauren E., Negre, Olivier, Lee, Ciaran M., Bao, GaVolume:
11
Language:
english
Journal:
Science Translational Medicine
DOI:
10.1126/scitranslmed.aaw3768
Date:
July, 2019
File:
PDF, 5.35 MB
english, 2019