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Effectiveness and safety of the tri-iodothyronine analogue Triac in children and adults with MCT8 deficiency: an international, single-arm, open-label, phase 2 trial
Groeneweg, Stefan, Peeters, Robin P, Moran, Carla, Stoupa, Athanasia, Auriol, Françoise, Tonduti, Davide, Dica, Alice, Paone, Laura, Rozenkova, Klara, Malikova, Jana, van der Walt, Adri, de Coo, IrenaLanguage:
english
Journal:
The Lancet Diabetes & Endocrinology
DOI:
10.1016/S2213-8587(19)30155-X
Date:
July, 2019
File:
PDF, 420 KB
english, 2019