Targeting GNE myopathy: A dual prodrug approach for the delivery of N-acetyl mannosamine 6-phosphate.
Morozzi, Chiara, Sedláková, Jana, Serpi, Michaela, Avigliano, Marialuce, Carbajo, Rosangela, Sandoval, Lucia, Valles-Ayoub, Yadira, Crutcher, Patrick J, Thomas, Stephen, Pertusati, FabrizioLanguage:
english
Journal:
Journal of Medicinal Chemistry
DOI:
10.1021/acs.jmedchem.9b00833
Date:
August, 2019
File:
PDF, 888 KB
english, 2019