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ND2 COST-UTILITY ANALYSIS OF SINGLE DOSE GENE-REPLACEMENT THERAPY FOR SPINAL MUSCULAR ATROPHY TYPE 1 COMPARED TO CHRONIC NUSINERSEN TREATMENT
Malone, D., Dean, R., Miller, B., Arjunji, R., Feltner, D.E., Sproule, D.M., Jensen, I.S., Maru, B., Dabbous, O.Volume:
22
Journal:
Value in Health
DOI:
10.1016/j.jval.2019.04.060
Date:
May, 2019
File:
PDF, 592 KB
2019