Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide
Kourkouta, Eleni, Weij, Rudie, González-Barriga, Anchel, Mulder, Melissa, Verheul, Ruurd, Bosgra, Sieto, Groenendaal, Bas, Puoliväli, Jukka, Toivanen, Jussi, van Deutekom, Judith C.T., Datson, NicoleVolume:
17
Journal:
Molecular Therapy - Nucleic Acids
DOI:
10.1016/j.omtn.2019.07.004
Date:
September, 2019
File:
PDF, 1.67 MB
2019