PND9 EVENT-FREE SURVIVAL AND MOTOR MILESTONE ACHIEVEMENT...

PND9 EVENT-FREE SURVIVAL AND MOTOR MILESTONE ACHIEVEMENT FOLLOWING AVXS-101 AND NUSINERSEN INTERVENTIONS CONTRASTED TO NATURAL HISTORY FOR TYPE I SPINAL MUSCULAR ATROPHY PATIENTS

Dabbous, O., Sproule, D.M., Feltner, D.E., Ogrinc, F.G., Menier, M., Droege, M., Maru, B., Khan, F., Arjunji, R.
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Volume:
22
Language:
english
Journal:
Value in Health
DOI:
10.1016/j.jval.2019.04.1282
Date:
May, 2019
File:
PDF, 383 KB
english, 2019
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