Post-transplant laronidase augmentation for children with Hurler syndrome: biochemical outcomes
Lund, Troy C., Miller, Weston P., Liao, Ai Yin, Tolar, Jakub, Shanley, Ryan, Pasquali, Marzia, Sando, Nicole, Bigger, Brian W., Polgreen, Lynda E., Orchard, Paul J.Volume:
9
Language:
english
Journal:
Scientific Reports
DOI:
10.1038/s41598-019-50595-1
Date:
December, 2019
File:
PDF, 1.30 MB
english, 2019