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Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease
Holthaus, Sophia-Martha kleine, Herranz-Martin, Saul, Massaro, Giulia, Aristorena, Mikel, Hoke, Justin, Hughes, Michael P, Maswood, Ryea, Semenyuk, Olha, Basche, Mark, Shah, Amna Z, Klaska, Izabela P,Language:
english
Journal:
Human Molecular Genetics
DOI:
10.1093/hmg/ddz210
Date:
September, 2019
File:
PDF, 1.58 MB
english, 2019