P.372CSF miRNAs as biomarkers to indicate the clinical response to Spinraza treatment for patients with spinal muscular atrophy
Doreste, B., Sanson, M., Zaharieva, I., Scoto, M., Muntoni, F., Zhou, H.Volume:
29
Journal:
Neuromuscular Disorders
DOI:
10.1016/j.nmd.2019.06.534
Date:
October, 2019
File:
PDF, 54 KB
2019