Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A
Pasi, K. John, Rangarajan, Savita, Mitchell, Nina, Lester, Will, Symington, Emily, Madan, Bella, Laffan, Michael, Russell, Chris B., Li, Mingjin, Pierce, Glenn F., Wong, Wing Y.Volume:
382
Journal:
New England Journal of Medicine
DOI:
10.1056/NEJMoa1908490
Date:
January, 2020
File:
PDF, 364 KB
2020