A reversible RNA on-switch that controls gene expression of AAV-delivered therapeutics in vivo
Zhong, Guocai, Wang, Haimin, He, Wenhui, Li, Yujun, Mou, Huihui, Tickner, Zachary J., Tran, Mai H., Ou, Tianling, Yin, Yiming, Diao, Huitian, Farzan, MichaelJournal:
Nature Biotechnology
DOI:
10.1038/s41587-019-0357-y
Date:
December, 2019
File:
PDF, 4.07 MB
2019