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A Case Report of a Japanese Boy with Morquio A Syndrome: Effects of Enzyme Replacement Therapy Initiated at the Age of 24 Months
Nakamura-Utsunomiya, Akari, Nakamae, Toshio, Kagawa, Reiko, Karakawa, Shuhei, Sakata, Sonoko, Sakura, Fumiaki, Tani, Chihiro, Matsubara, Yoshiko, Ishino, Takashi, Tajima, Go, Okada, SatoshiVolume:
21
Language:
english
Journal:
International Journal of Molecular Sciences
DOI:
10.3390/ijms21030989
Date:
February, 2020
File:
PDF, 1.87 MB
english, 2020