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Gene replacement ameliorates deficits in mouse and human models of cyclin-dependent kinase-like 5 disorder
Gao, Yunan, Irvine, Elaine E, Eleftheriadou, Ioanna, Naranjo, Carlos Jiménez, Hearn-Yeates, Francesca, Bosch, Leontien, Glegola, Justyna A, Murdoch, Leah, Czerniak, Aleksandra, Meloni, Ilaria, RenierJournal:
Brain
DOI:
10.1093/brain/awaa028
Date:
March, 2020
File:
PDF, 1.81 MB
2020