Voretigene Neparvovec-rzyl for Treatment of RPE65 -Mediated Inherited Retinal Diseases: A Model for Ocular Gene Therapy Development
Ciulla, Thomas A., Hussain, Rehan M., Berrocal, Audina M., Nagiel, AaronJournal:
Expert Opinion on Biological Therapy
DOI:
10.1080/14712598.2020.1740676
Date:
March, 2020
File:
PDF, 2.20 MB
2020