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Germline CRISPR/Cas9-mediated Gene Editing Prevents Vision Loss in a Novel Mouse Model of Aniridia
Mirjalili Mohanna, Seyedeh Zeinab, Hickmott, Jack W., Lam, Siu Ling, Chiu, Nina Y., Lengyell, Tess C., Tam, Beatrice M., Moritz, Orson L., Simpson, Elizabeth M.Language:
english
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2020.03.002
Date:
March, 2020
File:
PDF, 5.18 MB
english, 2020