Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy
Brendel, Christian, Negre, Olivier, Rothe, Michael, Guda, Swaroopa, Parsons, Geoff, Harris, Chad, McGuinness, Meaghan, Abriss, Daniela, Tsytsykova, Alla, Klatt, Denise, Bentler, Martin, Pellin, DaniloLanguage:
english
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2020.03.015
Date:
March, 2020
File:
PDF, 4.63 MB
english, 2020